Paying the Price
Yesterday was a historic day in the world of Duchenne. Sarepta Therapeutics announced that they’d finally received guidance from the FDA on… more
April 22, 2014
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This Plane Has Been Cleared For Takeoff
It’s old news by now…Sarepta’s exon-skipping drug, Eteplirsen, is safe and shows efficacy. If we siftthrough all the details, all… more
March 26, 2014
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What’s In A Number
Just 30 days ago, a small army of Duchenne parents and organizations launched a petition asking the White House to… more
March 26, 2014
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Send a Message to Save Lives
We have a problem, one that I never expected us to face. When we launched Team Joseph five years ago,… more
February 3, 2014
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